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Issue Date
Title
Author(s)
2005
Threshold effect of urinary glycosaminoglycans and the walk test as indicators of disease progression in a survey of subjects with mucopolysaccharidosis VI (Maroteaux-Lamy syndrome)
Swiedler, S.
;
Beck, M.
;
Bajbouj, M.
;
Giugliani, R.
;
Schwartz, I.
;
Harmatz, P.
;
Wraith, J.
;
Roberts, J.
;
Ketteridge, D.
;
Hopwood, J.
;
Guffon, N.
;
Miranda, C.
;
Teles, E.
;
Berger, K.
;
Piscia-Nichols, C.
Discover
Author
1
Bajbouj, M.
1
Beck, M.
1
Berger, K.
1
Giugliani, R.
1
Guffon, N.
1
Piscia-Nichols, C.
1
Schwartz, I.
1
Swiedler, S.
1
Wraith, J.
Subject
1
Adult
1
Data Interpretation, Statistical
1
Disease Progression
1
Health Surveys
1
Heart Function Tests
1
Male
1
Middle Aged
1
Quality of Life
1
Respiratory Function Tests
1
Surveys and Questionnaires
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Date issued
1
2005